SN38

SN38

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임상 약물 정보

영어 이름연구 코드연구 개발 단계회사적응증임상 시험
ALXN-2220ALXN2220; ALXN-2220; NI006; NI-006Phase 3 ClinicalAstraZeneca global R & D (China) Co Ltd
Cardiomyopathies; Transthyretin amyloidosis
상세
Nexiguran ziclumeranNTLA-2001Phase 3 ClinicalIntellia Therapeutics Inc
Amyloidosis, Familial; Amyloid Neuropathies, Familial; Peripheral Nervous System Diseases; Metabolism, Inborn Errors; Polyneuropathies; Genetic Diseases, Inborn; Metabolic Diseases; Cardiomyopathies; Amyloidosis; Nervous System Diseases; Neuromuscular Diseases; Heredodegenerative Disorders, Nervous System; Neurodegenerative Diseases; Amyloid Neuropathies; Transthyretin amyloidosis
상세
NNC6019-0001NNC6019-0001; NNC-6019; PRX-004Phase 2 ClinicalNovo Nordisk A/S
Cardiomyopathies; Transthyretin amyloidosis
상세
NI-006NI-006Phase 1 ClinicalNeurimmune Ag
Cardiomyopathies; Transthyretin amyloidosis
상세
NucresiranALNTTRsc-04Phase 1 ClinicalAlnylam Pharmaceuticals Inc
Transthyretin amyloidosis
상세

시판 약물 정보

영어 이름연구 코드연구 개발 단계회사가장 빠른 브랜드 이름가장 빠른 승인 국가가장 빠른 적응증가장 빠른 승인 회사가장 빠른 승인 날짜적응증임상 시험
PatisiranSAR-438037; GENZ-438027; ALN-TTR02; ALN-18328ApprovedAlnylam Pharmaceuticals IncOnpattroUnited StatesAmyloid Neuropathies, FamilialAlnylam Pharmaceuticals Inc2018-08-10
Amyloidosis, Familial; Amyloid Neuropathies, Familial; Polyneuropathies; Cardiomyopathies; Amyloidosis; Transthyretin amyloidosis; Amyloid Neuropathies
상세
VutrisiranALN-TTRSC02ApprovedAlnylam Pharmaceuticals IncAMVUTTRAUnited StatesAmyloid Neuropathies, Familial; Transthyretin amyloidosisAlnylam Pharmaceuticals Inc2022-06-13
Amyloidosis, Familial; Amyloid Neuropathies, Familial; Cardiomyopathies; Amyloidosis; Transthyretin amyloidosis
상세
AcoramidisAG-10; ALXN-2060; ALXN 2060; BBP-265ApprovedStanford UniversityAttrubyUnited StatesTransthyretin amyloidosisBridgebio Pharma Inc2024-11-22
Polyneuropathies; Heart Diseases; Cardiomyopathies; Amyloidosis; Transthyretin amyloidosis; Amyloid Neuropathies
상세
Inotersen sodiumISIS-420915; GSK-2998728ApprovedIonis Pharmaceuticals IncTegsediEUAmyloidosisAkcea Therapeutics Ireland Ltd2018-07-05
Adenomatous Polyposis Coli; Amyloid Neuropathies, Familial; Amyloidosis; Transthyretin amyloidosis
상세
TafamidisPF-6291826; Fx-1006A; PF-06291826; FX-1006AApprovedPfizer Inc维万心, VYNDAMAXUnited StatesHeart DiseasesFoldrx Pharmaceuticals Inc2019-05-03
Heart Diseases; Transthyretin amyloidosis
상세
EplontersenIONIS-TTR-LRx; AKCEA-TTR-LRx; ION-682884; ION-TTR-LRxApprovedIonis Pharmaceuticals IncWAINUAUnited StatesTransthyretin amyloidosisAstrazeneca Ab2023-12-21
Amyloid Neuropathies, Familial; Cardiomyopathies; Transthyretin amyloidosis
상세
Tafamidis MeglumineFX-1006A; PF-6291826; Fx-1006A; PF-06291826ApprovedPfizer Inc维达全, VyndaqelEUAmyloidosisPfizer Europe Ma Eeig2011-11-16
Amyloid Neuropathies, Familial; Immunoglobulin Light-chain Amyloidosis; Cardiomyopathies; Amyloidosis; Transthyretin amyloidosis; Amyloid Neuropathies
상세