| English Name | Research Code | Highest Development Stage | Company | Earliest Brand Name | Earliest Approval Country | Earliest Indication | Earliest Approval Company | Earliest Approval Date | Indication | Clinical Trial |
|---|---|---|---|---|---|---|---|---|---|---|
| Nitisinone | SC-0735; SYN-118; NTBC | Approved | Swedish Orphan Biovitrum Ag | Orfadin, Nityr | United States | Tyrosinemias | Swedish Orphan Biovitrum Ag | 2002-01-18 | Alkaptonuria; Blindness; Tyrosinemias; Albinism | Details |

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